Using Patient Specific iPSC-Cardiomyocytes for Disease Modeling
Ulrich Broeckel, MD
Tuesday, March 31, 2015
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Chapters
Introduction
Conflict of Interest
CONGRATULATIONS!
Generate data; Interpret data? Implement data?
Questions
Translational Precision Medicine
Next Steps Concept
Left Ventricular Hypertrophy
Study Population
iPS Derivation Status
CM Quality Parameters
Human Cardiomyocyte Model of Hypertrophy
HT Assay Platform
Protocol Development
First Round of Production Phenotyping: African American
miRNA and Cardiovascular Disease
miRNA Sequence Analysis
Knock Down: Predicted miRNAs
Knock Down: Expression Analysis
Variation Between Lines
Variation between iPSC-CM Lines
Develop Drug Screening Assay
Primary Screen at 5μM Hits >50% activity compared with Macitentan control
Develop Drug Screening Assay
Summary
Acknowledgement
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